CMTTdb

An integrated database for cancer molecular targeted thearpies

Entry Detail


General information
Database:DB00110
Objective:to assess the safety of the multikinase inhibitor regorafenib in patients with hepatocellular carcinoma (hepatocellular carcinoma) that had progressed following firstline sorafenib.
Authors:Bruix J, et al
Title:Regorafenib as secondline therapy for intermediate or advanced hepatocellular carcinoma: multicenter, openlabel, phase II safety study.
Journal:Eur J Cancer.
Year:2013
PMID:23809766
Trial Design
Clinical Trial Id:NCT01003015
Agent:regorafenib
Target:Protooncogene tyrosineprotein kinase receptor ret
Mast/stem cell growth factor receptor
Vascular endothelial growth factor receptor 2
Vascular endothelial growth factor receptor 3
Cancer Type:liver cancer
Cancer Subtype:hepatocellular carcinoma
Therapy Type:mono
Therapeutic Combination Type:NA
Therapeutic Combination Content:NA
Study Type:a multicentre, openlabel, phase II safety study.
Key Patients Feature:patients with Barcelona Clinic Liver Cancer stage B or C hepatocellular carcinoma and preserved to mildly impaired liver function (ChildPugh class A) at 13 centres in Europe and Asia
Biomarker:NA
Biomark Analysis:NA
Control Group Info:single arm
Treatment Info:pts received regorafenib 160 mg once daily in cycles of 3 weeks on/1 week off treatment until disease progression, unacceptable toxicity, death or patient/physician decision to discontinue.
Primary End Point:safety
Secondary End Point:efficacy (including time to progression and overall survival).
Patients Number:36
Trial Results
DLT_MTD:NA
Objective Response Rate:The median treatment duration was 19.5 weeks (range 2103). At data cutoff, 3 patients remained on treatment. Reasons for discontinuation were adverse events (n=20), disease progression (n=10), consent withdrawal (n=2) and death (n=1). 17 patients required dose reductions (mostly for adverse events [n=15]); 35 patients had treatment interruption (mostly for adverse events [n=32] or patient error [n=11]).
Disease Control Rate:NA
Median Time to Progression:NA
Median PFS A vs. C:Median time to progression was 4.3 months
Median OS A vs. C:Median overall survival was 13.8 months.
Adverse Event(agent arm):The most frequent treatmentrelated adverse events were handfoot skin reaction (any grade n=19; grade more than and equal to 3 n=5), diarrhoea (n=19; n=2), fatigue (n=19; n=6), hypothyroidism (n=15; n=0), anorexia (n=13; n=0), hypertension (n=13; n=1), nausea (n=12; n=0) and voice changes (n=10; n=0).
Conclusions:Regorafenib had acceptable tolerability and evidence of antitumour activity in patients with intermediate or advanced hepatocellular carcinoma that progressed following firstline sorafenib.