CMTTdb

An integrated database for cancer molecular targeted thearpies

Entry Detail


General information
Database:DB00931
Objective:Thisphase II study of sorafenib, an oral multikinase inhibitor that targets Raf kinase and receptor tyrosine kinases, assessed efficacy, toxicity, pharmacokinetics, and biomarkers in advanced hepatocellular carcinoma (hepatocellular carcinoma) patients.
Authors:AbouAlfa GK, et al
Title:Phase II study of sorafenib in patients with advanced hepatocellular carcinoma.
Journal:J Clin Oncol.
Year:2006
PMID:16908937
Trial Design
Clinical Trial Id:NA
Agent:sorafenib
Target:Vascular endothelial growth factor receptor 1
BRaf protooncogene serine/threonineprotein kinase
Protooncogene tyrosineprotein kinase receptor ret
Cancer Type:liver cancer
Cancer Subtype:advanced hepatocellular carcinoma
Therapy Type:mono
Therapeutic Combination Type:NA
Therapeutic Combination Content:NA
Study Type:Phase II study
Key Patients Feature:Patients with inoperable hepatocellular carcinoma, no prior systemic treatment, and ChildPugh (CP) A or B
Biomarker:phosphorylated extracellular signal regulated kinase (pERK) in pretreatment biopsies (immunohistochemistry) and bloodcell RNA expression patterns in selected patients
Biomark Analysis:There were no significant pharmacokinetic differences between CP A and B patients. Pretreatment tumor pERK levels correlated with TTP.
Control Group Info:single arm
Treatment Info:pts received continuous, oral sorafenib 400 mg bid in 4week cycles
Primary End Point:efficacy, toxicity, pharmacokinetics, and biomarkers
Secondary End Point:NA
Patients Number:137
Trial Results
DLT_MTD:NA
Objective Response Rate:8%
Disease Control Rate:41.60%
Median Time to Progression: 4.2 months
Median PFS A vs. C:NA
Median OS A vs. C: 9.2 months
Adverse Event(agent arm):The most common drugrelated adverse events (any grade) were dermatologic, constitutional, and GI (Table 5). Grade 3 toxicities included fatigue (9.5%), diarrhea (8.0%), and HFS (5.1%).
Conclusions: Although singleagent sorafenib has modest efficacy in hepatocellular carcinoma, the manageable toxicity and mechanisms of action support a role for combination regimens with other anticancer agents.